WebA Phase 3, Multicenter, Open-Label Extension Study of Phenoptin in Subjects With PKU Who Have Elevated Phenylalanine Levels. Latest version (submitted August 18, 2009) on ClinicalTrials.gov ... The primary objective of this trial is to evaluate the safety and tolerability of long-term Phenoptin treatment in subjects with PKU. Detailed ... WebJan 26, 2006 · Phenoptin is an investigational oral small molecule therapeutic for the treatment of PKU. The active ingredient in Phenoptin, sapropterin dihydrochloride, is the synthetic form of 6R-BH4, a naturally occurring enzyme cofactor. BioMarin received orphan drug designation for Phenoptin to treat PKU from both the FDA and European Medicines …
BioMarin’s Shares Move On Phenoptin Phase III Success
WebJul 19, 2006 · The purpose of this study is to evaluate the ability of Phenoptin to control blood phenylalanine levels in subjects who have hyperphenylalaninemia due to a prim... English Dansk Deutsch English Español Français Italiano Magyar Nederlands Norsk Polski Português Suomi Svenska Čeština Русский 日本語 简体中文 한국어 WebOct 14, 2005 · The AEDs, including carbamazepine, oxcarbazepine, phenytoin, ethosuximide, gabapentin, divalproex sodium, topiramate, and others, are used as first-line therapy in … cozumel broadview hts ohio
National Center for Biotechnology Information
WebNov 22, 2004 · BioMarin Pharmaceutical Inc. (Nasdaq and SWX: BMRN) announced today that it has entered into a strategic business partnership with Daiichi Suntory Pharma Co., Ltd., for Phenoptin (TM) (sapropterin hydrochloride), an investigational oral enzyme cofactor for the treatment of the genetic disease phenylketonuria (PKU). WebThe Effect of Nursing Empowerment Program Evaluation of Phe Fluctuation in PKU Pts Treated With PKU GOLIKE Versus Standard Amino Acid Protein Substitute. Preliminary Study of Brain Effects of Palynziq-Related Changes in Phenylalanine in Individuals With PKU Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With … WebJan 17, 2007 · Merck Serono and its US partner BioMarin have presented promising late-stage data for Phenoptin, their new experimental treatment for phenylketonuria, a genetic disorder which causes excessive build-up of an amino acid in the blood. - News - … cozumel boat snorkel